Misfolded SOD1 associated with motor neuron mitochondria alters mitochondrial shape and distribution prior to clinical onset - PubMed (original) (raw)
Misfolded SOD1 associated with motor neuron mitochondria alters mitochondrial shape and distribution prior to clinical onset
Christine Vande Velde et al. PLoS One. 2011.
Abstract
Mutations in superoxide dismutase (SOD1) are causative for inherited amyotrophic lateral sclerosis. A proportion of SOD1 mutant protein is misfolded onto the cytoplasmic face of mitochondria in one or more spinal cord cell types. By construction of mice in which mitochondrially targeted enhanced green fluorescent protein is selectively expressed in motor neurons, we demonstrate that axonal mitochondria of motor neurons are primary in vivo targets for misfolded SOD1. Mutant SOD1 alters axonal mitochondrial morphology and distribution, with dismutase active SOD1 causing mitochondrial clustering at the proximal side of Schmidt-Lanterman incisures within motor axons and dismutase inactive SOD1 producing aberrantly elongated axonal mitochondria beginning pre-symptomatically and increasing in severity as disease progresses. Somal mitochondria are altered by mutant SOD1, with loss of the characteristic cylindrical, networked morphology and its replacement by a less elongated, more spherical shape. These data indicate that mutant SOD1 binding to mitochondria disrupts normal mitochondrial distribution and size homeostasis as early pathogenic features of SOD1 mutant-mediated ALS.
Conflict of interest statement
Competing Interests: The authors have declared that no competing interests exist.
Figures
Figure 1. Generation of a novel transgenic mouse with mitochondria labeled uniquely in motor neurons.
(A) Schematic of Hb9-MitoEGFP transgene. (B) Immunoblot of spinal cord homogenates of Hb9-MitoEGFP founders (F34, F17, F36, F20) and F34 sublines probed for EGFP and tubulin (loading control). (C–G) MitoEGFP (green) expression in spinal cord motor neurons (C & D), sciatic nerve (E), and L5 motor axons (F & G) labeled with SMI32 (C, red), cytochrome c (D & F, red), and Fluoromyelin Red (F & G, blue/red). Note that mitochondria have typical tubular and punctate morphologies and MitoEGFP expression is excluded from Schwann cells. (G & H) 15% of large caliber (>4.5 µm) L5 motor axons express MitoEGFP in 12 months animal. The expected biphasic distribution of axonal caliber in adult C57Bl/6 mice is indicated in the upper right corner. Comparison of axonal and somal mitochondrial length (I), width (J) and aspect ratio (K) in Hb9-MitoEGFP mice. Scale bars, 10 µm.
Figure 2. Misfolded SOD1 associates with motor neuron axonal mitochondria in vivo.
An antibody raised against misfolded SOD1 (A5C3, red) labels ventral (A) but not dorsal (B) axons of 10 month SOD1G85R mouse. Myelin Basic Protein (MBP, blue) is included as a counter-label. Misfolded SOD1 (A5C3, red) is often colocalized with mitochondria (EGFP, green) in motor axons of both SOD1G85R (C & D) and SOD1G37R animals (E & F) but not non-SOD1 MitoEGFP littermates (H). Regions of the spinal cord, consistent with axonal exit zones also demonstrate double-labeling (G). The boundaries of individual axons are indicated either by MBP labeling (blue) or dotted lines. Scale bars are as indicated.
Figure 3. Motor neuron mitochondria are rounder in mutant SOD1 mice.
MitoEGFP (green) expression in spinal cord motor neurons in control MitoEGFP (A) and SOD1G37R early symptomatic animals (B–D). The control neuron has normal mitochondria of diverse shapes and sizes. In contrast, SOD1G37R motor neurons have rounded swollen mitochondria with uneven distribution. Arrows indicate possible axon hillocks. Motor neuron boundaries have been outlined with dotted line. Quantification of mitochondrial length (E) and aspect ratio (F) in motor neuron cell bodies of mutant SOD1 animals of various ages and age-matched MitoEGFP control animals. ***, p<0.0005. Scale bars, 10 µm.
Figure 4. Distributions of mitochondrial morphology and distribution.
Distributions in various morphological parameters of somal (A–D) and axonal (E–H) mitochondria. Bins for area (A,E) are 0–0.25, 0.26–0.50, 0.51–0.75, 0.76–1.0, and >1.0 µm2. Bins for length (B,F) are 0–1, 1.01–2, 2.01–3, 3.01–4, and >4 µm. Bins for aspect ratio (C,G) are 1–2, 2.01–4, 4.01–6, 6.01–8, and >8. Bins for width (D,H) are 0–0.25, 0.26–0.50, 0.51–0.75, 0.76–1.0, and >1.0 µm. Statistics have been calculated using Chi-square with Yates' correction for continuity and significant differences in distributions are indicated: *, p<0.05; **, p<0.005; ***, p<0.0005.
Figure 5. Mitochondria morphology is altered in mutant SOD1 axons.
MitoEGFP (green) expressed in the sciatic nerves in control (A), asymptomatic SOD1G85R 7 months (B and C), SOD1G85R 8 months (D and E), and SOD1G37R early symptomatic (F and G) labeled with Fluoromyelin red (red). Round and evenly distributed mitochondria are seen in both SOD1G85R (symptomatic stage) and SOD1G37R (early symptomatic stage). Mitochondria `pile-up or clusters are also seen in the proximal side of SLIs (arrows) in the SOD1G37R axons. Arrowheads indicate “strings” of mitochondria. Arrows indicate SLIs (H) Schematic indicating proximal and distal locations of SLIs. Mitochondrial area (I), length (J), aspect ratio (K), and density (L) were evaluated in motor axons of the sciatic nerves of and mutant SOD1 animals of various ages and age-matched MitoEGFP control animals, as described in detail in the Materials and Methods. Statistics are indicated: *, p<0.05; **, p<0.005; ***, p<0.0005.
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References
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