Neural progenitor cell engraftment corrects lysosomal storage throughout the MRS VII mouse brain (original) (raw)

References

  1. Snyder, E. Y. et al. Cell 68, 33–51 (1992).
    Article CAS Google Scholar
  2. Snyder, E. Y. Semin. Perinatol. 16, 106–121 (1992).
    CAS PubMed Google Scholar
  3. Snyder, E. Y., Yandava, B. D., Pan, Z-H., Yoon, C. & Macklis, J. D. Soc. Neurosci. Abstrs. 19, 613 (1993).
    Google Scholar
  4. Macklis, J. D., Yoon, C. H. & Snyder, E. Y. Expl Neurol. 129, 9 (1994).
    Google Scholar
  5. Renfranz, P. J., Cunningham, M. G. & McKay, R. D. G. Cell 66, 713–719 (1991).
    Article CAS Google Scholar
  6. Groves, A. K. et al. Nature 362, 453–455 (1993).
    Article ADS CAS Google Scholar
  7. Onnifer, S. M., Whittemore, S. R. & Holets, V. R. Expl Neurol. 122, 130–142 (1993).
    Article Google Scholar
  8. Sly, W. S., Quinton, B. A., McAlister, W. H. & Rimoin, D. L. J. Pediatr. 82, 249–257 (1973).
    Article CAS Google Scholar
  9. Haskins, M. E., Desnick, R. J., DiFerrante, N., Jezyk, P. F. & Patterson, D. F. Pediatr. Res. 18, 980–984 (1984).
    CAS PubMed Google Scholar
  10. Birkenmeier, E. H. et al. J. clin. Invest. 83, 1258–1266 (1989).
    Article CAS Google Scholar
  11. Neufeld, E. F. & Muenzer, J. in The Metabolic Basis of Inherited Disease 7th edn (eds Scriver, C. R., Beaudet, A. L., Sly, W. S. & Valle, D.) 2465–2494 (McGraw Hill, New York, 1995).
    Google Scholar
  12. Haskins, M. E. et al. in Treatment of Genetic Diseases (ed. Desnick, R. J.) 183–202 (Churchill Livingstone, New York, 1991).
    Google Scholar
  13. Birkenmeier, E. H. et al. Blood 78, 3081–3092 (1991).
    CAS PubMed Google Scholar
  14. Wolfe, J. H. et al. Nature 360, 749–753 (1992).
    Article ADS CAS Google Scholar
  15. Wolfe, J. H., Deshmane, S. L. & Fraser, N. W. Nature Genet. 1, 379–384 (1992).
    Article CAS Google Scholar
  16. Sands, M. S. et al. Lab. Invest. 68, 676–686 (1993).
    CAS PubMed Google Scholar
  17. Moullier, P., Bohl, D., Heard, J.-M. & Danos, O. Nature Genet. 4, 154–159 (1993).
    Article CAS Google Scholar
  18. Marechal, V., Naffakh, N., Danos, O. & Heard, J.-M. Blood 82, 1358–1365 (1993).
    CAS PubMed Google Scholar
  19. Vogler, C. et al. Pediat. Res. 34, 837–840 (1993).
    Article CAS Google Scholar
  20. Sands, M. S. et al. J. clin. Invest. 93, 2324–2331 (1994).
    Article ADS CAS Google Scholar
  21. Ryder, E. F., Snyder, E. Y. & Cepko, C. L. J. Neurobiol. 21, 356–375 (1990).
    Article CAS Google Scholar
  22. Kitchens, D. L., Snyder, E. Y. & Gottlieb, D. I. J. Neurobiol. 25, 797–807 (1994).
    Article CAS Google Scholar
  23. Altman, J. J. comp. Neurol. 137, 433–458 (1969).
    Article CAS Google Scholar
  24. Vogler, C. et al. Am. J. Path. 136, 207–217 (1990).
    CAS PubMed Google Scholar
  25. Wolfe, J. H. et al. Proc. natn. Acad. Sci. U.S.A. 87, 2877–2881 (1990).
    Article ADS CAS Google Scholar
  26. Sands, M. S. & Birkenmeier, E. H. Proc. natn. Acad. Sci. U.S.A. 90, 6567–6571 (1993).
    Article ADS CAS Google Scholar
  27. Kyle, J. W. et al. Proc natn. Acad. Sci. U.S.A. 87, 3914–3918 (1990).
    Article ADS CAS Google Scholar
  28. Wolfe, J. H. et al. Gene Ther. 2, 70–78 (1995).
    CAS PubMed Google Scholar
  29. Taylor, R. M. & Wolfe, J. H. Expl Cell Res. 214, 606–613 (1994).
    Article CAS Google Scholar
  30. Christie, D. et al. Arch. Dis. Child 70, 275–280 (1994).
    Article CAS Google Scholar
  31. Suhr, S. & Gage, F. H. Arch. Neurol. 50, 1252–1268 (1993).
    Article CAS Google Scholar
  32. Breakefield, X. O. Nature Genet. 3, 187–189 (1993).
    Article CAS Google Scholar
  33. Fisher, L. J. & Gage, F. H. FASEB J. 8, 489–496 (1994).
    Article CAS Google Scholar
  34. Anton, R. et al. Expl Neurol. 127, 207–218 (1994).
    Article CAS Google Scholar

Download references