Cerebral hypomyelination associated with biallelic variants of FIG4 (original) (raw)

Congenital CNS Hypomyelination in the Fig4 Null Mouse Is Rescued by Neuronal Expression of the PI(3,5)P2 Phosphatase Fig4

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Journal of Neuroscience, 2011

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Karl Lovblad

Pediatric Neurology, 2000

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Emilia Bellone

Annals of Neurology, 1999

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Shin Nabatame

American Journal of Medical Genetics Part A, 2013

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Dominant inheritance of cerebral gigantism

Jean Soto

Journal of Pediatrics, 1977

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Novel TUBB4A mutations and expansion of the neuroimaging phenotype of hypomyelination with atrophy of the basal ganglia and cerebellum (H-ABC)

Carlos Ferreira

American Journal of Medical Genetics Part A, 2014

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Clinical Phenotypes of Different (P) Mutations May Include Charcot?Marie?Tooth Type 1B, Dejerine?Sottas, and Congenital Hypomyelination

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Neuron, 1996

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Severe Hypomyelination of the Murine CNS in the Absence of Myelin-Associated Glycoprotein and Fyn Tyrosine Kinase

Melitta Schachner

The Journal of Neuroscience

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A syndrome of congenital microcephaly, intellectual disability and dysmorphism with a homozygous mutation in FRMD4A

ilan Shelef

European journal of human genetics : EJHG, 2014

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Chris Walsh Children's

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TGIF Mutations in Human Holoprosencephaly: Correlation between Genotype and Phenotype

Gordon Gowans

Molecular Syndromology, 2010

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Diffuse hypomyelination is not obligate for POLR3-related disorders

Kether Guerrero

Neurology, 2016

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Spinocerebellar degeneration and cerebral hypomyelination in a family

Leo Wolansky

American Journal of Medical Genetics, 1995

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Clinical Spectrum of SIX3-Associated Mutations In Holoprosencephaly: Correlation Between Genotype, Phenotype, and Function

P. Njolstad

British Medical …, 2009

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TUBB4A de novo mutations cause isolated hypomyelination

Guy Helman, Geneviève Bernard

Neurology, 2014

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Brain Abnormalities in Patients with Germline Variants in H3F3: Novel Imaging Findings and Neurologic Symptoms Beyond Somatic Variants and Brain Tumors

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American Journal of Neuroradiology, 2022

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Reduced Cerebral White Matter Integrity Assessed by DTI in Cognitively Normal H63D-HFE Polymorphism Carriers

Mark Meadowcroft

Journal of Neuroimaging, 2017

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Foetal onset of EIF2B related disorder in two siblings: cerebellar hypoplasia with absent Bergmann glia and severe hypomyelination

Fanny Sauvestre

Acta Neuropathologica Communications, 2020

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Deficiency of hyccin, a newly identified membrane protein, causes hypomyelination and congenital cataract

Marina Pedemonte

Nature Genetics, 2006

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New syndrome characterized by hypomyelination with atrophy of the basal ganglia and cerebellum

Marjo Van Der Knaap

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Hypomyelination and Congenital Cataract: Identification of a Novel likely pathogenic c.414+1G>A in FAM126A gene Variant

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Clinical Case Reports, 2021

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Hypomyelination caused by a novel homozygous pathogenic variant in FOLR1: complete clinical and radiological recovery with oral folinic acid therapy and review of the literature

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