Organic aciduria in neonatal multiple carboxylase deficiency (original) (raw)

Biotin-sensitive 3-methylcrotonylglycinuria in a patient with severe growth delay, ectodermal abnormalities, neonatal progeroid appearance, and developmental delay

R. Wevers

Clinical Dysmorphology, 2008

View PDFchevron_right

Holocarboxylase synthetase deficiency: A biotin-responsive organic acidemia

John Foreman

The Journal of Pediatrics, 1980

View PDFchevron_right

Pyruvate carboxylase deficiencies: Complementation studies between “French” and “American” phenotypes in cultured fibroblasts

C. Augereau

Journal of Inherited Metabolic Disease, 1985

View PDFchevron_right

Biotin-responsive immunoregulatory dysfunction in multiple carboxylase deficiency

C. Griscelli

Journal of Clinical Immunology, 1982

View PDFchevron_right

Isolated 3-Methylcrotonyl-CoA Carboxylase Deficiency: Evidence for an Allele-Specific Dominant Negative Effect and Responsiveness to Biotin Therapy

David Valle

The American Journal of Human Genetics, 2004

View PDFchevron_right

3-methylcrotonyl-CoA carboxylase deficiency: Clinical, biochemical, enzymatic and molecular studies in 88 individuals

Sarah Grünert

Orphanet Journal of Rare Diseases, 2012

View PDFchevron_right

Biochemical and molecular characterization of 3-Methylcrotonylglycinuria in an Italian asymptomatic girl

Giulia Frisso

Genetics and Molecular Biology

View PDFchevron_right

Biotin and biotinidase deficiency

Subhashinee Wijeratne

Expert Review of Endocrinology & Metabolism, 2008

View PDFchevron_right

The Molecular Basis of 3-Methylcrotonylglycinuria, a Disorder of Leucine Catabolism

Olga Criado, Lourdes Desviat

The American Journal of Human Genetics, 2001

View PDFchevron_right

Pyruvate carboxylase responsive to ketosis in a multiple carboxylase deficiency patient

Victoria Castillo

Journal of Inherited Metabolic Disease, 1986

View PDFchevron_right

Urinary Excretion of 3-Hydroxyisovaleric Acid and 3-Hydroxyisovaleryl Carnitine Increases in Response to a Leucine Challenge in Marginally Biotin-Deficient Humans

Horace Spencer

The Journal of Nutrition, 2011

View PDFchevron_right

Biotin dependency due to a defect in biotin transport

Rebecca Mardach

Journal of Clinical Investigation, 2002

View PDFchevron_right

Early infantile presentation of 3-methylcrotonyl CoA carboxylase deficiency: a case report

Anuragsingh Chandel

International Journal of Contemporary Pediatrics, 2021

View PDFchevron_right

Leukodystrophy and CSF Purine Abnormalities Associated with Isolated 3-Methylcrotonyl-CoA Carboxylase Deficiency

Alexandra Latini

Metabolic brain …, 2002

View PDFchevron_right

Biotinidase deficiency

ramdas dahiphale

Indian pediatrics, 2008

View PDFchevron_right

Prospective ascertainment of complete and partial serum biotinidase deficiency in the newborn

B. Lemieux

1989

View PDFchevron_right

Glutaric aciduria type II: Biochemical investigation and treatment of a child diagnosed prenatally

Paul Engel

Journal of Inherited Metabolic Disease, 1984

View PDFchevron_right

Mechanism of Biotin Responsiveness in Biotin-Responsive Multiple Carboxylase Deficiency

Eric Campeau

Molecular Genetics and Metabolism, 1999

View PDFchevron_right

Differential Effects of Biotin Deficiency and Replenishment on Rat Liver Pyruvate and Propionyl-CoA Carboxylases and on Their mRNAs

Martha Andrade

Molecular Genetics and Metabolism, 1999

View PDFchevron_right

The Molecular Basis of Human 3-Methylcrotonyl-CoA Carboxylase Deficiency

David Valle

Journal of Clinical …, 2001

View PDFchevron_right

Differential Effects of Biotin Deficiency and Replenishment on Rat Liver Pyruvate and Propionyl-CoA Carboxylases and on Their MRNAs* 1

martha andrade

Molecular genetics and …, 1999

View PDFchevron_right

Case report of early biotinidase deficiency, a type of multiple carboxylase deficiency

Mohammed Siddiq

International Journal of Contemporary Pediatrics, 2021

View PDFchevron_right

Kinetic Characterization of Mutations Found in Propionic Acidemia and Methylcrotonylglycinuria: EVIDENCE FOR COOPERATIVITY IN BIOTIN CARBOXYLASE

Grover Waldrop

Journal of Biological Chemistry, 2004

View PDFchevron_right

Molecular mechanism of dominant expression in 3‐methylcrotonyl‐CoA carboxylase deficiency

Matthias Baumgartner

Journal of Inherited Metabolic Disease, 2005

View PDFchevron_right