Oligosaccharide excretion in adult Gaucher disease (original) (raw)

Conditions affecting the activity of glucocerebrosidase purified fom spleens of control subjects and patients with type 1 Gaucher disease

Sonja Van Weely

Biochimica et Biophysica Acta (BBA) - Protein Structure and Molecular Enzymology, 1990

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Glycolipid analysis of different tissues and cerebrospinal fluid in type II Gaucher disease

Bruno Bembi

2002

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Therapeutic response to intravenous infusions of glucocerebrosidase in a patient with Gaucher disease

Gary Murray

Proceedings of the National Academy of Sciences, 1990

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Enzyme replacement therapy in Gaucher's disease: a rapid, high-yield method for purification of glucocerebrosidase

Joseph Shiloach

Proceedings of the National Academy of Sciences, 1976

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Glucosylsphingosine Accumulation in Mice and Patients with Type 2 Gaucher Disease Begins Early in Gestation

Brian Martin, Ellen Sidransky

Pediatric Research, 2000

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Activity of glucocerebrosidase in extracts of different cell types from type 1 Gaucher disease patients

Sonja Van Weely

Clinical Genetics, 2008

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Clinical phenotype of Gaucher disease in relation to properties of mutant glucocerebrosidase in cultured fibroblasts

Sonja Van Weely

Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease, 1991

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Ultrastructural localization of glucocerebrosidase in cultured Gaucher's disease fibroblasts by immunocytochemistry

Arnold Reuser

Journal of Neurology, 1987

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Cellular Uptake of Glucocerebrosidase in Gaucher Patients Receiving Enzyme Replacement Treatment

Matilde Merino Sanjuan

Clinical Pharmacokinetics, 2016

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Enzyme replacement therapy for mild patients with Gaucher disease

Ari Zimran

American Journal of Hematology, 2009

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Immunological and isoelectric focusing study of β-glucocerebrosidase from normal and Gaucher disease

Britta Hardy

Biochemical and Biophysical Research Communications, 1984

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Enzymic diagnosis in 27 cases with Gaucher's disease

Klaus Harzer

Clinica Chimica Acta, 1980

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Diagnosis of Lysosomal Storage Disorders: Gaucher Disease

Angela Dajnoki

Current Protocols in Human Genetics, 2001

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Histological characterisation of visceral changes in a patient with type 2 Gaucher disease treated with enzyme replacement therapy

Tatsuhiko Miyazaki

Blood cells, molecules & diseases, 2016

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Quantification of glucosylceramide in plasma of Gaucher disease patients

Luciene Vianna, Maria Muller

Brazilian Journal of Pharmaceutical Sciences, 2010

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Characterization of glucocerebrosidase in Greek Gaucher disease patients: mutation analysis and biochemical studies

Helen Michelakakis

Journal of Inherited Metabolic Disease, 1995

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Biochemical properties of β-glucosidase in leukocytes from patients and obligated heterozygotes for Gaucher disease carriers

Roberto Giugliani

Clinica Chimica Acta, 2005

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Enzyme replacement treatment in type 1 and type 3 Gaucher's disease

Bruno Bembi

The Lancet, 1994

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Role of pH in determining the cell-type-specific residual activity of glucocerebrosidase in type 1 Gaucher disease

Sonja Van Weely

Journal of Clinical Investigation, 1993

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Biosynthesis and maturation of glucocerebrosidase in Gaucher fibroblasts

Gary Murray

European Journal of Biochemistry, 1987

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Relationship between Glucocerebrosidase Activity and clinical response to Enzyme Replacement Therapy in patients with Gaucher Disease type I

Vicente Giner

Basic & clinical pharmacology & toxicology, 2018

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Clinico-hematological profile of lysosomal storage disorders — a report of three cases

Aparna Harbhajanka

Indian Journal of Hematology and Blood Transfusion, 2008

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Management of non-neuronopathic Gaucher disease with special reference to pregnancy, splenectomy, bisphosphonate therapy, use of biomarkers and bone disease monitoring

Ana Martins

Journal of Inherited Metabolic Disease, 2008

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Modifying exogenous glucocerebrosidase for effective replacement therapy in Gaucher disease

Gary Murray

Journal of Inherited Metabolic Disease, 1994

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Reduced glucosylceramide in the mouse model of Fabry disease: Correction by successful enzyme replacement therapy

Daniel Rodrigues

Gene, 2014

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Elevated plasma glucosylsphingosine in Gaucher disease: relation to phenotype, storage cell markers, and therapeutic response

Maria Lucia G Ferraz

Blood, 2011

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Screening for lysosomal diseases in a selected pediatric population: the case of Gaucher disease and acid sphingomyelinase deficiency

Simona Fecarotta

Orphanet Journal of Rare Diseases, 2023

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Enzyme replacement therapy in type 1 Gaucher disease and a review of the literature

Gökhan Kabaçam

Turkish Journal of Haematology

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Plasmalogen levels in Gaucher disease

Theodoros Marinakis

Blood Cells, Molecules, and Diseases, 2008

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