Pleiotropic Effects of CEP290 (NPHP6) Mutations Extend to Meckel Syndrome (original) (raw)

Molecular genetics of Meckel syndrome: Ciliary genes are defective in MKS

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2009

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CEP290 Mutations Are Frequently Identified in the Oculo-Renal Form of Joubert Syndrome–Related Disorders

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Novel human pathological mutations

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Mutations in TMEM216 perturb ciliogenesis and cause Joubert, Meckel and related syndromes

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Faculty of 1000 evaluation for Mutations in PNKP cause microcephaly, seizures and defects in DNA repair

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