Progressive Infantile Neurodegeneration Caused by 2-Methyl-3-Hydroxybutyryl-CoA Dehydrogenase Deficiency: A Novel Inborn Error of Branched-Chain Fatty Acid and Isoleucine Metabolism (original) (raw)

Mutations in the Gene Encoding 3-Hydroxyisobutyryl-CoA Hydrolase Results in Progressive Infantile Neurodegeneration

Ference Loupatty

The American Journal of Human Genetics, 2007

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Spastic diplegia and periventricular white matter abnormalities in 2-methyl-3-hydroxybutyryl-CoA dehydrogenase deficiency, a defect of isoleucine metabolism: differential diagnosis with hypoxic–ischemic brain diseases

rob ofman

Molecular Genetics and Metabolism, 2004

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2-Methyl-3-Hydroxybutyryl-CoA Dehydrogenase (MHBD) Deficiency: An X-linked Inborn Error of Isoleucine Metabolism that May Mimic a Mitochondrial Disease

Magdalena Ugarte, Jaime Dalmau

Pediatric Research, 2005

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Microcephaly and developmental delay caused by short-chain acyl-CoA dehydrogenase deficiency

Saliha Senel

The Turkish journal of pediatrics, 2017

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3-Hydroxyisobutyryl-CoA Hydrolase Deficiency in a Turkish Child with a Novel HIBCH Gene Mutation and Literature Review

Fatma Çolak

2020

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2-methylbutyryl-CoA dehydrogenase deficiency associated with autism and mental retardation: a case report

Bjørn Tvedt

Journal of Medical Case Reports, 2007

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Enzymes of Fatty Acid β‐Oxidation in Developing Brain

D. Dewey

Journal of Neurochemistry, 1988

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2Methyl3-Hydroxybutyryl-CoA Dehydrogenase Deficiency Is Caused by Mutations in the HADH2 Gene

Johannes Zschocke

American Journal of Human Genetics, 2003

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Short-chain acyl-CoA dehydrogenase (SCAD) deficiency: An examination of the medical and neurodevelopmental characteristics of 14 cases identified through newborn screening or clinical symptoms

Susan Waisbren

Molecular Genetics and Metabolism, 2008

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Early infantile presentation of 3-methylcrotonyl CoA carboxylase deficiency: a case report

anurag chandel

International Journal of Contemporary Pediatrics, 2021

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Neurocognitive assessments and long-term outcome in an adult with 2-methyl-3-hydroxybutyryl-CoA dehydrogenase deficiency

philomena mccarthy

Molecular Genetics and Metabolism Reports, 2018

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Stroke-like encephalopathy in an infant with 3-hydroxy-3-methylglutaryl-coenzyme A lyase deficiency

Ronald Wanders

European Journal of Pediatrics, 1998

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2-Methylbutyryl-coenzyme A dehydrogenase deficiency: Functional and molecular studies on a defect in isoleucine catabolism

Andre Megarbane

Molecular Genetics and Metabolism, 2008

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A novel mutation in medium chain acyl-CoA dehydrogenase causes sudden neonatal death

Harold Sims

Journal of Clinical Investigation, 1994

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Early Neonatal Diagnosis of Long-Chain 3-Hydroxyacyl Coenzyme A Dehydrogenase and Mitochondrial Trifunctional Protein Deficiencies

Michael Bennett

Molecular Genetics and Metabolism, 2002

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Medium-chain acyl-CoA dehydrogenase deficiency does not correlate with apparent life-threatening events and the sudden infant death syndrome: results from phenylpropionate loading tests and DNA analysis

F. Zacchello

European Journal of Pediatrics, 1994

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Biochemical, molecular, and clinical characteristics of children with short chain acyl-CoA dehydrogenase deficiency detected by newborn screening in California

Julie Neidich

Molecular genetics and metabolism, 2012

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Prospective Diagnosis of 2-Methylbutyryl-CoA Dehydrogenase Deficiency in the Hmong Population by Newborn Screening Using Tandem Mass Spectrometry

Chester Whitley

PEDIATRICS, 2003

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Neonatal onset of medium-chain Acyl-CoA dehydrogenase deficiency in two siblings

Fumio Endo

Brain and Development, 1988

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Evidence that the major metabolites accumulating in medium-chain acyl-CoA dehydrogenase deficiency disturb mitochondrial energy homeostasis in rat brain

Gustavo Ferreira

Brain Research, 2009

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Multiple sources of metabolic disturbance in ETHE1-related ethylmalonic encephalopathy

Anne Vassault, Pascale Lonlay

Journal of Inherited Metabolic Disease, 2010

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